Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
![An urgent need for improving thalassemia care due to the wide gap in current real-life practice and clinical practice guidelines | Scientific Reports An urgent need for improving thalassemia care due to the wide gap in current real-life practice and clinical practice guidelines | Scientific Reports](https://media.springernature.com/full/springer-static/image/art%3A10.1038%2Fs41598-021-92715-w/MediaObjects/41598_2021_92715_Fig1_HTML.png)
An urgent need for improving thalassemia care due to the wide gap in current real-life practice and clinical practice guidelines | Scientific Reports
Replacing the suppressed hormone: toward a better treatment for iron overload in β-thalassemia major? | Haematologica
Sirolimus for Treatment of β-Thalassemia: From Pre-Clinical Studies to the Design of Clinical Trials
![Guidelines for the Management of Transfusion-Dependent Thalassaemia (4th Edition - Version 2.0) by Thalassaemia International Federation (TIF) - Issuu Guidelines for the Management of Transfusion-Dependent Thalassaemia (4th Edition - Version 2.0) by Thalassaemia International Federation (TIF) - Issuu](https://image.isu.pub/220523125456-31254084c0fc681ef531a9580454bbd7/jpg/page_1.jpg)
Guidelines for the Management of Transfusion-Dependent Thalassaemia (4th Edition - Version 2.0) by Thalassaemia International Federation (TIF) - Issuu
![Quality of life in patients with β‐thalassemia: A prospective study of transfusion‐dependent and non‐transfusion‐dependent patients in Greece, Italy, Lebanon, and Thailand - Cappellini - 2019 - American Journal of Hematology - Wiley Quality of life in patients with β‐thalassemia: A prospective study of transfusion‐dependent and non‐transfusion‐dependent patients in Greece, Italy, Lebanon, and Thailand - Cappellini - 2019 - American Journal of Hematology - Wiley](https://onlinelibrary.wiley.com/cms/asset/a3ab599c-f810-44a4-8d26-916b998a40ec/ajh.25584.fp.png)
Quality of life in patients with β‐thalassemia: A prospective study of transfusion‐dependent and non‐transfusion‐dependent patients in Greece, Italy, Lebanon, and Thailand - Cappellini - 2019 - American Journal of Hematology - Wiley
![Advances in genome editing: the technology of choice for precise and efficient β-thalassemia treatment | Gene Therapy Advances in genome editing: the technology of choice for precise and efficient β-thalassemia treatment | Gene Therapy](https://media.springernature.com/m685/springer-static/image/art%3A10.1038%2Fs41434-020-0153-9/MediaObjects/41434_2020_153_Fig1_HTML.png)
Advances in genome editing: the technology of choice for precise and efficient β-thalassemia treatment | Gene Therapy
![Biomolecules | Free Full-Text | Epigenetic Insights and Potential Modifiers as Therapeutic Targets in β–Thalassemia Biomolecules | Free Full-Text | Epigenetic Insights and Potential Modifiers as Therapeutic Targets in β–Thalassemia](https://www.mdpi.com/biomolecules/biomolecules-11-00755/article_deploy/html/images/biomolecules-11-00755-g001.png)
Biomolecules | Free Full-Text | Epigenetic Insights and Potential Modifiers as Therapeutic Targets in β–Thalassemia
![IJMS | Free Full-Text | Non-Transfusion-Dependent Thalassemia: An Update on Complications and Management IJMS | Free Full-Text | Non-Transfusion-Dependent Thalassemia: An Update on Complications and Management](https://www.mdpi.com/ijms/ijms-19-00182/article_deploy/html/images/ijms-19-00182-g001.png)
IJMS | Free Full-Text | Non-Transfusion-Dependent Thalassemia: An Update on Complications and Management
![2021 update on clinical trials in β‐thalassemia - Musallam - 2021 - American Journal of Hematology - Wiley Online Library 2021 update on clinical trials in β‐thalassemia - Musallam - 2021 - American Journal of Hematology - Wiley Online Library](https://onlinelibrary.wiley.com/cms/asset/caf537f7-2fd6-410b-9f9e-4bd2bf79cd29/ajh26316-fig-0001-m.jpg)
2021 update on clinical trials in β‐thalassemia - Musallam - 2021 - American Journal of Hematology - Wiley Online Library
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
![Safety and efficacy of thalidomide in patients with transfusion-dependent β- thalassemia: a randomized clinical trial | Signal Transduction and Targeted Therapy Safety and efficacy of thalidomide in patients with transfusion-dependent β- thalassemia: a randomized clinical trial | Signal Transduction and Targeted Therapy](https://media.springernature.com/full/springer-static/image/art%3A10.1038%2Fs41392-021-00811-0/MediaObjects/41392_2021_811_Fig1_HTML.png)
Safety and efficacy of thalidomide in patients with transfusion-dependent β- thalassemia: a randomized clinical trial | Signal Transduction and Targeted Therapy
![Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells](https://www.frontiersin.org/files/Articles/730873/fphar-12-730873-HTML/image_m/fphar-12-730873-g002.jpg)
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
![Significance of genetic modifiers of hemoglobinopathies leading towards precision medicine | Scientific Reports Significance of genetic modifiers of hemoglobinopathies leading towards precision medicine | Scientific Reports](https://media.springernature.com/full/springer-static/image/art%3A10.1038%2Fs41598-021-00169-x/MediaObjects/41598_2021_169_Fig1_HTML.png)
Significance of genetic modifiers of hemoglobinopathies leading towards precision medicine | Scientific Reports
![Diseases | Free Full-Text | Luspatercept: A New Tool for the Treatment of Anemia Related to β-Thalassemia, Myelodysplastic Syndromes and Primary Myelofibrosis Diseases | Free Full-Text | Luspatercept: A New Tool for the Treatment of Anemia Related to β-Thalassemia, Myelodysplastic Syndromes and Primary Myelofibrosis](https://www.mdpi.com/diseases/diseases-10-00085/article_deploy/html/images/diseases-10-00085-g001.png)